How genetic therapies transformed the lives of sickle cell patients
Their stories are divided into before and after. First, those long years of pain which flooded every moment—school, relationships, work.
Mar 18, 2024
0
0
Their stories are divided into before and after. First, those long years of pain which flooded every moment—school, relationships, work.
Mar 18, 2024
0
0
UdeM's Stéphanie Forté and co-researchers in Canada and Brazil have shown how people with sickle cell disease or sickle cell trait have a higher chance of dying from COVID-19 than the general population.
Feb 29, 2024
0
1
Gene therapy has allowed several children born with inherited deafness to hear.
Jan 28, 2024
0
27
A modeling study comparing the cost-effectiveness of gene therapy versus common care for patients with sickle cell disease found that gene therapy is beneficial in this patient population and likely cost-effective if the ...
Jan 22, 2024
0
0
Cornell researchers have taken an important step toward harnessing CRISPR gene editing in "targeted, safe and potent" cancer treatment, according to Ailong Ke, professor of chemistry and chemical biology in the College of ...
Jan 22, 2024
0
0
After approving Casgevy (exagamglogene autotemcel) in December to treat sickle cell disease, the U.S. Food and Drug Administration announced Tuesday that the therapy has now been approved to treat patients older than 12 years ...
Jan 17, 2024
0
0
Lyric Porter wanted her life back. Born with sickle cell disease, she had a fever at age 5 that scarred her lungs and required her to roll an oxygen tank to school. When she was growing up, clogged blood vessels racked her ...
Jan 3, 2024
0
0
Gautam Dongre's two children in India and Pascazia Mazeze's son in Tanzania live with an inherited blood disorder that turns blood cells into instruments of pain.
Dec 14, 2023
1
26
Patients with sickle cell disease (SCD) often face a reduced quality of life and a lower life expectancy. Allotransplantation, the first treatment for SCD with curative potential, comes with risks, including transplant-related ...
Dec 11, 2023
0
0
The United States on Friday approved a breakthrough therapy that uses revolutionary gene editing tool CRISPR to treat the debilitating blood disorder sickle cell disease.
Dec 8, 2023
0
3